Invention Grant
- Patent Title: Antisense nucleic acids
-
Application No.: US15122435Application Date: 2015-03-11
-
Publication No.: US09988629B2Publication Date: 2018-06-05
- Inventor: Tatsushi Wakayama , Haruna Seo , Youhei Satou , Shin'ichi Takeda , Tetsuya Nagata
- Applicant: NIPPON SHINYAKU CO., LTD. , NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY
- Applicant Address: JP Kyoto-shi, Kyoto JP Kodaira-shi, Tokyo
- Assignee: NIPPON SHINYAKU CO., LTD.,NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY
- Current Assignee: NIPPON SHINYAKU CO., LTD.,NATIONAL CENTER OF NEUROLOGY AND PSYCHIATRY
- Current Assignee Address: JP Kyoto-shi, Kyoto JP Kodaira-shi, Tokyo
- Agency: Drinker Biddle & Reath LLP
- Priority: JP2014-048897 20140312
- International Application: PCT/JP2015/057180 WO 20150311
- International Announcement: WO2015/137409 WO 20150917
- Main IPC: C12N15/113
- IPC: C12N15/113 ; A61K31/713 ; C12N15/11

Abstract:
Provided is a drug that allows highly-efficient skipping of exon 51 in the human dystrophin gene. The present invention provides an antisense oligomer which enables exon 51 in the human dystrophin gene to be skipped.
Public/Granted literature
- US20170067048A1 ANTISENSE NUCLEIC ACIDS Public/Granted day:2017-03-09
Information query
IPC分类: