Invention Grant
- Patent Title: Compounds for nonsense suppression, and methods for their use
- Patent Title (中): 用于废物抑制的化合物及其使用方法
-
Application No.: US14263478Application Date: 2014-04-28
-
Publication No.: US09273076B2Publication Date: 2016-03-01
- Inventor: Jeffrey A. Campbell , Atiyya Kahn , James Takasugi , Ellen Welch
- Applicant: PTC Therapeutics, Inc.
- Applicant Address: US NJ South Plainfield
- Assignee: PTC Therapeutics, Inc.
- Current Assignee: PTC Therapeutics, Inc.
- Current Assignee Address: US NJ South Plainfield
- Agency: Hoffmann & Baron, LLP
- Main IPC: A61K31/675
- IPC: A61K31/675 ; A61K31/535 ; A61K31/497 ; A61K31/505 ; A61K31/445 ; A61K31/41 ; C07F9/653 ; C07D231/12 ; C07D233/64 ; C07D249/08 ; C07D261/08 ; C07D263/32 ; C07D271/06 ; C07D277/30 ; C07D285/12 ; C07D307/68 ; C07D333/24 ; C07D413/12
Abstract:
The present invention relates to methods, compounds, and compositions for treating or preventing diseases associated with nonsense mutations in an mRNA by administering the compounds or compositions of the present invention. More particularly, the present invention relates to methods, compounds, and compositions for suppressing premature translation termination associated with a nonsense mutation in an mRNA.
Public/Granted literature
- US20140235586A1 COMPOUNDS FOR NONSENSE SUPPRESSION, AND METHODS FOR THEIR USE Public/Granted day:2014-08-21
Information query
